{"id":9413,"date":"2026-03-19T12:03:53","date_gmt":"2026-03-19T11:03:53","guid":{"rendered":"https:\/\/ern-ithaca.eu\/?post_type=news&#038;p=9413"},"modified":"2026-03-19T12:03:53","modified_gmt":"2026-03-19T11:03:53","slug":"new-mooc-launch-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases","status":"publish","type":"news","link":"https:\/\/ern-ithaca.eu\/de\/events-news\/news\/new-mooc-launch-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\/","title":{"rendered":"Start eines neuen MOOC: Von der DNA zur Heilung \u2013 Gen- und genmodifizierte Zelltherapien f\u00fcr seltene Krankheiten"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Da es f\u00fcr \u00fcber 95% seltener Krankheiten noch immer keine zugelassenen Therapien gibt, besteht ein dringender Bedarf an spezialisierter Ausbildung im Bereich der Therapeutika der n\u00e4chsten Generation. Um diese L\u00fccke zu schlie\u00dfen, freut sich die Stiftung f\u00fcr seltene Krankheiten (FFRD) bekannt zu geben, dass sie ihr neues <strong>Massive Open Online Course (MOOC) auf FutureLearn: \u201cVon der DNA zur Heilung: Gen- und genmodifizierte Zelltherapien f\u00fcr seltene Krankheiten.\u201d<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Dieser Kurs, der von der FFRD koordiniert und mit Unterst\u00fctzung des ASGCT &amp; Pfizer Global Medical Education Grant entwickelt wurde, bringt international anerkannte Experten zusammen, um den Teilnehmern die neuesten Technologien n\u00e4herzubringen, die die medizinische Landschaft grundlegend ver\u00e4ndern.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Zu den wichtigsten Themen geh\u00f6ren:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>Genbearbeitung: CRISPR-Cas9, Basenbearbeitung und Prime-Editing<\/li>\n\n\n\n<li>RNA-Therapeutika: mRNA und Antisense-Oligonukleotide (ASOs)<\/li>\n\n\n\n<li>Verabreichungssysteme: Virale Vektoren und nicht-virale Systeme<\/li>\n\n\n\n<li>Auswirkungen in der Praxis: Klinische Fallstudien zu H\u00e4mophilie und Stoffwechselerkrankungen sowie bewegende Erfahrungsberichte von Patienten<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">Die Anmeldung ist ab sofort m\u00f6glich: https:\/\/www.futurelearn.com\/courses\/from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Der Zugriff auf die Inhalte ist in den ersten drei Wochen nach der Anmeldung kostenlos. A<strong> moderierte Sitzung <\/strong>findet vom 16. M\u00e4rz bis zum 8. Mai statt. W\u00e4hrend dieser Zeit stehen Experten online zur Verf\u00fcgung, um Fragen zu beantworten und die Lernenden in Echtzeit zu unterst\u00fctzen.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Dieser Kurs richtet sich in erster Linie an<strong>\u00a0Studierende und Nachwuchswissenschaftler aus den Bereichen Biologie, Biowissenschaften und Medizin<\/strong>. Es k\u00f6nnte auch f\u00fcr Fachkr\u00e4fte im Gesundheitswesen, politische Entscheidungstr\u00e4ger, Vertreter der Industrie, Patientenvertreter und alle anderen von Interesse sein, die ein besseres Verst\u00e4ndnis f\u00fcr die Entwicklung von Gen- und genmodifizierten Zelltherapien f\u00fcr seltene Krankheiten erlangen m\u00f6chten. Grundkenntnisse in Biologie werden empfohlen.<\/p>","protected":false},"excerpt":{"rendered":"<p>With over 95% of rare diseases still lacking approved treatments, there is a pressing need for specialized education in next-generation therapeutics. To address this gap, the Foundation for Rare Diseases (FFRD) is excited to announce the launch of their new Massive Open Online Course (MOOC) on FutureLearn: \u201cFrom DNA to Cure: Gene and Gene-Modified Cell [&hellip;]<\/p>\n","protected":false},"featured_media":0,"template":"","categories":[],"tags":[],"class_list":["post-9413","news","type-news","status-publish","hentry"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v28.7 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>New MOOC Launch: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases - ERN ITHACA<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/ern-ithaca.eu\/de\/events-news\/news\/new-mooc-launch-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\/\" \/>\n<meta property=\"og:locale\" content=\"de_DE\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"New MOOC Launch: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases - ERN ITHACA\" \/>\n<meta property=\"og:description\" content=\"With over 95% of rare diseases still lacking approved treatments, there is a pressing need for specialized education in next-generation therapeutics. 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