{"id":9645,"date":"2026-04-20T11:12:47","date_gmt":"2026-04-20T09:12:47","guid":{"rendered":"https:\/\/ern-ithaca.eu\/?post_type=news&#038;p=9645"},"modified":"2026-04-20T11:12:47","modified_gmt":"2026-04-20T09:12:47","slug":"new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases","status":"publish","type":"news","link":"https:\/\/ern-ithaca.eu\/de\/events-news\/news\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\/","title":{"rendered":"Neues MOOC: Von der DNA zur Heilung \u2013 Gen- und genmodifizierte Zelltherapien f\u00fcr seltene Krankheiten"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Da es f\u00fcr \u00fcber 95% seltene Krankheiten noch immer keine zugelassenen Therapien gibt, besteht ein dringender Bedarf an spezialisierter Ausbildung im Bereich der Therapeutika der n\u00e4chsten Generation. Um diese L\u00fccke zu schlie\u00dfen, hat die\u00a0<strong>Stiftung f\u00fcr seltene Krankheiten (FFRD)<\/strong>\u00a0startet seinen neuen Massive Open Online Course (MOOC) am\u00a0<strong>FutureLearn<\/strong>:\u00a0<strong>\u201cVon der DNA zur Heilung: Gen- und genmodifizierte Zelltherapien f\u00fcr seltene Krankheiten.\u201d<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Koordiniert von der FFRD und entwickelt mit Unterst\u00fctzung der&nbsp;<strong>ASGCT- und Pfizer-Zuschuss f\u00fcr globale medizinische Fortbildung<\/strong>, dieser Kurs vereint&nbsp;<strong>international anerkannte Experten<\/strong>&nbsp;um den Teilnehmern einen \u00dcberblick \u00fcber die neuesten Technologien zu geben, die die medizinische Landschaft grundlegend ver\u00e4ndern.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Zu den wichtigsten Themen geh\u00f6ren:<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>Geneditierung:<\/strong>\u00a0CRISPR-Cas9, Base Editing und Prime Editing<\/li>\n\n\n\n<li><strong>RNA-Therapeutika:<\/strong>\u00a0mRNA und Antisense-Oligonukleotide (ASOs)<\/li>\n\n\n\n<li><strong>Verabreichungssysteme:<\/strong>\u00a0Virale Vektoren und nicht-virale Systeme<\/li>\n<\/ul>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>Auswirkungen in der Praxis:<\/strong>\u00a0Klinische Fallstudien zu H\u00e4mophilie und Stoffwechselst\u00f6rungen sowie bewegende Erfahrungsberichte von Patienten<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Die Anmeldung ist ab sofort m\u00f6glich:\u00a0<\/strong><a href=\"https:\/\/www.futurelearn.com\/courses\/from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\" target=\"_blank\" rel=\"noreferrer noopener\">https:\/\/www.futurelearn.com\/courses\/from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><br>Der Zugriff auf die Inhalte ist\u00a0<strong>In den ersten drei Wochen nach der Anmeldung kostenlos<\/strong>. Eine moderierte Sitzung dauert von\u00a0<strong>16. M\u00e4rz bis 8. Mai<\/strong>. W\u00e4hrend dieser Zeit stehen Experten online zur Verf\u00fcgung, um Fragen zu beantworten und die Lernenden in Echtzeit zu unterst\u00fctzen.<br><br>Dieser Kurs richtet sich in erster Linie an\u00a0<strong>Studierende und Nachwuchswissenschaftler<\/strong>\u00a0in der Biologie, den Lebenswissenschaften und der Medizin. Es k\u00f6nnte auch von Interesse sein f\u00fcr\u00a0<strong>Fachkr\u00e4fte im Gesundheitswesen, politische Entscheidungstr\u00e4ger, Vertreter der Industrie, Patientenvertreter<\/strong>, sowie alle, die mehr \u00fcber die Entwicklung von Gen- und genmodifizierten Zelltherapien f\u00fcr seltene Krankheiten erfahren m\u00f6chten. A\u00a0<strong>Grundkenntnisse in Biologie<\/strong>\u00a0wird empfohlen.<\/p>","protected":false},"excerpt":{"rendered":"<p>With over 95% of rare diseases still lacking approved treatments, there is a pressing need for specialized education in next-generation therapeutics. To address this gap, the\u00a0Foundation for Rare Diseases (FFRD)\u00a0is launching its new Massive Open Online Course (MOOC) on\u00a0FutureLearn:\u00a0\u201cFrom DNA to Cure: Gene and Gene-Modified Cell Therapies for Rare Diseases.\u201d Coordinated by FFRD and developed [&hellip;]<\/p>\n","protected":false},"featured_media":0,"template":"","categories":[],"tags":[],"class_list":["post-9645","news","type-news","status-publish","hentry"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v28.8 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>New MOOC: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases - ERN ITHACA<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/ern-ithaca.eu\/de\/events-news\/news\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\/\" \/>\n<meta property=\"og:locale\" content=\"de_DE\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"New MOOC: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases - ERN ITHACA\" \/>\n<meta property=\"og:description\" content=\"With over 95% of rare diseases still lacking approved treatments, there is a pressing need for specialized education in next-generation therapeutics. To address this gap, the\u00a0Foundation for Rare Diseases (FFRD)\u00a0is launching its new Massive Open Online Course (MOOC) on\u00a0FutureLearn:\u00a0\u201cFrom DNA to Cure: Gene and Gene-Modified Cell Therapies for Rare Diseases.\u201d Coordinated by FFRD and developed [&hellip;]\" \/>\n<meta property=\"og:url\" content=\"https:\/\/ern-ithaca.eu\/de\/events-news\/news\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\/\" \/>\n<meta property=\"og:site_name\" content=\"ERN ITHACA\" \/>\n<meta name=\"twitter:card\" content=\"summary_large_image\" \/>\n<meta name=\"twitter:site\" content=\"@ERNIthaca\" \/>\n<meta name=\"twitter:label1\" content=\"Gesch\u00e4tzte Lesezeit\" \/>\n\t<meta name=\"twitter:data1\" content=\"1\u00a0Minute\" \/>\n<script type=\"application\/ld+json\" class=\"yoast-schema-graph\">{\"@context\":\"https:\\\/\\\/schema.org\",\"@graph\":[{\"@type\":\"WebPage\",\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/events-news\\\/news\\\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\\\/\",\"url\":\"https:\\\/\\\/ern-ithaca.eu\\\/events-news\\\/news\\\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\\\/\",\"name\":\"New MOOC: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases - ERN ITHACA\",\"isPartOf\":{\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/#website\"},\"datePublished\":\"2026-04-20T09:12:47+00:00\",\"breadcrumb\":{\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/events-news\\\/news\\\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\\\/#breadcrumb\"},\"inLanguage\":\"de\",\"potentialAction\":[{\"@type\":\"ReadAction\",\"target\":[\"https:\\\/\\\/ern-ithaca.eu\\\/events-news\\\/news\\\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\\\/\"]}]},{\"@type\":\"BreadcrumbList\",\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/events-news\\\/news\\\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\\\/#breadcrumb\",\"itemListElement\":[{\"@type\":\"ListItem\",\"position\":1,\"name\":\"Home\",\"item\":\"https:\\\/\\\/ern-ithaca.eu\\\/\"},{\"@type\":\"ListItem\",\"position\":2,\"name\":\"NEWS & EVENTS > NEWS\",\"item\":\"https:\\\/\\\/ern-ithaca.eu\\\/events-news\\\/news\\\/\"},{\"@type\":\"ListItem\",\"position\":3,\"name\":\"New MOOC: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases\"}]},{\"@type\":\"WebSite\",\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/#website\",\"url\":\"https:\\\/\\\/ern-ithaca.eu\\\/\",\"name\":\"ERN ITHACA\",\"description\":\"WELCOME TO ERN-ITHACA WEBSITE!\",\"publisher\":{\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/#organization\"},\"potentialAction\":[{\"@type\":\"SearchAction\",\"target\":{\"@type\":\"EntryPoint\",\"urlTemplate\":\"https:\\\/\\\/ern-ithaca.eu\\\/?s={search_term_string}\"},\"query-input\":{\"@type\":\"PropertyValueSpecification\",\"valueRequired\":true,\"valueName\":\"search_term_string\"}}],\"inLanguage\":\"de\"},{\"@type\":\"Organization\",\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/#organization\",\"name\":\"ERN-ITHACA\",\"url\":\"https:\\\/\\\/ern-ithaca.eu\\\/\",\"logo\":{\"@type\":\"ImageObject\",\"inLanguage\":\"de\",\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/#\\\/schema\\\/logo\\\/image\\\/\",\"url\":\"https:\\\/\\\/ern-ithaca.eu\\\/wp-content\\\/uploads\\\/2022\\\/02\\\/Logo-ERN-ITHACA.jpg\",\"contentUrl\":\"https:\\\/\\\/ern-ithaca.eu\\\/wp-content\\\/uploads\\\/2022\\\/02\\\/Logo-ERN-ITHACA.jpg\",\"width\":454,\"height\":172,\"caption\":\"ERN-ITHACA\"},\"image\":{\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/#\\\/schema\\\/logo\\\/image\\\/\"},\"sameAs\":[\"https:\\\/\\\/x.com\\\/ERNIthaca\",\"https:\\\/\\\/www.linkedin.com\\\/company\\\/ithaca-european-reference-network-on-congenital-malformations-ans-rare-intellectual-disability\\\/?viewAsMember=true\"]}]}<\/script>\n<!-- \/ Yoast SEO plugin. -->","yoast_head_json":{"title":"New MOOC: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases - ERN ITHACA","robots":{"index":"index","follow":"follow","max-snippet":"max-snippet:-1","max-image-preview":"max-image-preview:large","max-video-preview":"max-video-preview:-1"},"canonical":"https:\/\/ern-ithaca.eu\/de\/events-news\/news\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\/","og_locale":"de_DE","og_type":"article","og_title":"New MOOC: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases - ERN ITHACA","og_description":"With over 95% of rare diseases still lacking approved treatments, there is a pressing need for specialized education in next-generation therapeutics. 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