{"id":9645,"date":"2026-04-20T11:12:47","date_gmt":"2026-04-20T09:12:47","guid":{"rendered":"https:\/\/ern-ithaca.eu\/?post_type=news&#038;p=9645"},"modified":"2026-04-20T11:12:47","modified_gmt":"2026-04-20T09:12:47","slug":"new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases","status":"publish","type":"news","link":"https:\/\/ern-ithaca.eu\/es\/events-news\/news\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\/","title":{"rendered":"Nuevo MOOC: \u00abDel ADN a la cura\u00bb: terapias g\u00e9nicas y con c\u00e9lulas modificadas gen\u00e9ticamente para enfermedades raras"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Dado que m\u00e1s de 95% de enfermedades raras siguen sin contar con tratamientos aprobados, existe una necesidad apremiante de formaci\u00f3n especializada en terapias de \u00faltima generaci\u00f3n. Para subsanar esta carencia, el\u00a0<strong>Fundaci\u00f3n para las Enfermedades Raras (FFRD)<\/strong>\u00a0va a lanzar su nuevo curso en l\u00ednea masivo y abierto (MOOC) sobre\u00a0<strong>FutureLearn<\/strong>:\u00a0<strong>\u201cDel ADN a la cura: terapias g\u00e9nicas y con c\u00e9lulas modificadas gen\u00e9ticamente para enfermedades raras\u201d.\u201d<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Coordinado por la FFRD y elaborado con el apoyo de la&nbsp;<strong>Beca de formaci\u00f3n m\u00e9dica global de la ASGCT y Pfizer<\/strong>, este curso re\u00fane a&nbsp;<strong>expertos de prestigio internacional<\/strong>&nbsp;para orientar a los participantes sobre las \u00faltimas tecnolog\u00edas que est\u00e1n transformando el panorama m\u00e9dico.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Entre los temas principales se incluyen:<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>Edici\u00f3n gen\u00e9tica:<\/strong>\u00a0CRISPR-Cas9, edici\u00f3n de bases y edici\u00f3n \u00abprime\u00bb<\/li>\n\n\n\n<li><strong>Terapias con ARN:<\/strong>\u00a0ARNm y oligonucle\u00f3tidos antisentido (ASO)<\/li>\n\n\n\n<li><strong>Sistemas de suministro:<\/strong>\u00a0Vectores virales y sistemas no virales<\/li>\n<\/ul>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>Repercusi\u00f3n en la vida real:<\/strong>\u00a0Estudios de casos cl\u00ednicos sobre hemofilia y trastornos metab\u00f3licos, junto con conmovedores testimonios de pacientes<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Ya est\u00e1 abierto el plazo de inscripci\u00f3n:\u00a0<\/strong><a href=\"https:\/\/www.futurelearn.com\/courses\/from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\" target=\"_blank\" rel=\"noreferrer noopener\">https:\/\/www.futurelearn.com\/courses\/from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><br>El acceso al contenido es\u00a0<strong>gratis durante las tres primeras semanas tras la inscripci\u00f3n<\/strong>. Una sesi\u00f3n guiada dura desde\u00a0<strong>Del 16 de marzo al 8 de mayo<\/strong>. Durante este tiempo, habr\u00e1 expertos disponibles en l\u00ednea para responder a las preguntas y ayudar a los alumnos en tiempo real.<br><br>Este curso est\u00e1 dirigido principalmente a\u00a0<strong>estudiantes universitarios e investigadores que inician su carrera profesional<\/strong>\u00a0en biolog\u00eda, ciencias de la vida y medicina. Tambi\u00e9n puede resultar de inter\u00e9s para\u00a0<strong>profesionales sanitarios, responsables pol\u00edticos, representantes del sector y defensores de los pacientes<\/strong>, y para cualquiera que desee comprender mejor el desarrollo de terapias g\u00e9nicas y de c\u00e9lulas modificadas gen\u00e9ticamente para enfermedades raras. A\u00a0<strong>conocimientos b\u00e1sicos de biolog\u00eda<\/strong>\u00a0Se recomienda.<\/p>","protected":false},"excerpt":{"rendered":"<p>With over 95% of rare diseases still lacking approved treatments, there is a pressing need for specialized education in next-generation therapeutics. To address this gap, the\u00a0Foundation for Rare Diseases (FFRD)\u00a0is launching its new Massive Open Online Course (MOOC) on\u00a0FutureLearn:\u00a0\u201cFrom DNA to Cure: Gene and Gene-Modified Cell Therapies for Rare Diseases.\u201d Coordinated by FFRD and developed [&hellip;]<\/p>\n","protected":false},"featured_media":0,"template":"","categories":[],"tags":[],"class_list":["post-9645","news","type-news","status-publish","hentry"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v28.8 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>New MOOC: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases - ERN ITHACA<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/ern-ithaca.eu\/es\/events-news\/news\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\/\" \/>\n<meta property=\"og:locale\" content=\"es_ES\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"New MOOC: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases - ERN ITHACA\" \/>\n<meta property=\"og:description\" content=\"With over 95% of rare diseases still lacking approved treatments, there is a pressing need for specialized education in next-generation therapeutics. To address this gap, the\u00a0Foundation for Rare Diseases (FFRD)\u00a0is launching its new Massive Open Online Course (MOOC) on\u00a0FutureLearn:\u00a0\u201cFrom DNA to Cure: Gene and Gene-Modified Cell Therapies for Rare Diseases.\u201d Coordinated by FFRD and developed [&hellip;]\" \/>\n<meta property=\"og:url\" content=\"https:\/\/ern-ithaca.eu\/es\/events-news\/news\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\/\" \/>\n<meta property=\"og:site_name\" content=\"ERN ITHACA\" \/>\n<meta name=\"twitter:card\" content=\"summary_large_image\" \/>\n<meta name=\"twitter:site\" content=\"@ERNIthaca\" \/>\n<meta name=\"twitter:label1\" content=\"Tiempo de lectura\" \/>\n\t<meta name=\"twitter:data1\" content=\"1 minuto\" \/>\n<script type=\"application\/ld+json\" class=\"yoast-schema-graph\">{\"@context\":\"https:\\\/\\\/schema.org\",\"@graph\":[{\"@type\":\"WebPage\",\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/events-news\\\/news\\\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\\\/\",\"url\":\"https:\\\/\\\/ern-ithaca.eu\\\/events-news\\\/news\\\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\\\/\",\"name\":\"New MOOC: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases - ERN ITHACA\",\"isPartOf\":{\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/#website\"},\"datePublished\":\"2026-04-20T09:12:47+00:00\",\"breadcrumb\":{\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/events-news\\\/news\\\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\\\/#breadcrumb\"},\"inLanguage\":\"es\",\"potentialAction\":[{\"@type\":\"ReadAction\",\"target\":[\"https:\\\/\\\/ern-ithaca.eu\\\/events-news\\\/news\\\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\\\/\"]}]},{\"@type\":\"BreadcrumbList\",\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/events-news\\\/news\\\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\\\/#breadcrumb\",\"itemListElement\":[{\"@type\":\"ListItem\",\"position\":1,\"name\":\"Home\",\"item\":\"https:\\\/\\\/ern-ithaca.eu\\\/\"},{\"@type\":\"ListItem\",\"position\":2,\"name\":\"NEWS & EVENTS > NEWS\",\"item\":\"https:\\\/\\\/ern-ithaca.eu\\\/events-news\\\/news\\\/\"},{\"@type\":\"ListItem\",\"position\":3,\"name\":\"New MOOC: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases\"}]},{\"@type\":\"WebSite\",\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/#website\",\"url\":\"https:\\\/\\\/ern-ithaca.eu\\\/\",\"name\":\"ERN ITHACA\",\"description\":\"WELCOME TO ERN-ITHACA WEBSITE!\",\"publisher\":{\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/#organization\"},\"potentialAction\":[{\"@type\":\"SearchAction\",\"target\":{\"@type\":\"EntryPoint\",\"urlTemplate\":\"https:\\\/\\\/ern-ithaca.eu\\\/?s={search_term_string}\"},\"query-input\":{\"@type\":\"PropertyValueSpecification\",\"valueRequired\":true,\"valueName\":\"search_term_string\"}}],\"inLanguage\":\"es\"},{\"@type\":\"Organization\",\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/#organization\",\"name\":\"ERN-ITHACA\",\"url\":\"https:\\\/\\\/ern-ithaca.eu\\\/\",\"logo\":{\"@type\":\"ImageObject\",\"inLanguage\":\"es\",\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/#\\\/schema\\\/logo\\\/image\\\/\",\"url\":\"https:\\\/\\\/ern-ithaca.eu\\\/wp-content\\\/uploads\\\/2022\\\/02\\\/Logo-ERN-ITHACA.jpg\",\"contentUrl\":\"https:\\\/\\\/ern-ithaca.eu\\\/wp-content\\\/uploads\\\/2022\\\/02\\\/Logo-ERN-ITHACA.jpg\",\"width\":454,\"height\":172,\"caption\":\"ERN-ITHACA\"},\"image\":{\"@id\":\"https:\\\/\\\/ern-ithaca.eu\\\/#\\\/schema\\\/logo\\\/image\\\/\"},\"sameAs\":[\"https:\\\/\\\/x.com\\\/ERNIthaca\",\"https:\\\/\\\/www.linkedin.com\\\/company\\\/ithaca-european-reference-network-on-congenital-malformations-ans-rare-intellectual-disability\\\/?viewAsMember=true\"]}]}<\/script>\n<!-- \/ Yoast SEO plugin. -->","yoast_head_json":{"title":"New MOOC: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases - ERN ITHACA","robots":{"index":"index","follow":"follow","max-snippet":"max-snippet:-1","max-image-preview":"max-image-preview:large","max-video-preview":"max-video-preview:-1"},"canonical":"https:\/\/ern-ithaca.eu\/es\/events-news\/news\/new-mooc-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\/","og_locale":"es_ES","og_type":"article","og_title":"New MOOC: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases - ERN ITHACA","og_description":"With over 95% of rare diseases still lacking approved treatments, there is a pressing need for specialized education in next-generation therapeutics. 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