{"id":9413,"date":"2026-03-19T12:03:53","date_gmt":"2026-03-19T11:03:53","guid":{"rendered":"https:\/\/ern-ithaca.eu\/?post_type=news&#038;p=9413"},"modified":"2026-03-19T12:03:53","modified_gmt":"2026-03-19T11:03:53","slug":"new-mooc-launch-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases","status":"publish","type":"news","link":"https:\/\/ern-ithaca.eu\/fr\/events-news\/news\/new-mooc-launch-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\/","title":{"rendered":"Lancement d'un nouveau MOOC : \u00ab De l'ADN au traitement : th\u00e9rapies g\u00e9niques et cellulaires g\u00e9n\u00e9tiquement modifi\u00e9es pour les maladies rares \u00bb"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Avec plus de 95% de maladies rares pour lesquelles il n'existe toujours pas de traitements approuv\u00e9s, il existe un besoin urgent de formations sp\u00e9cialis\u00e9es dans les th\u00e9rapies de nouvelle g\u00e9n\u00e9ration. Afin de combler cette lacune, la Fondation pour les maladies rares (FFRD) a le plaisir d'annoncer le lancement de son nouveau <strong>Cours en ligne ouvert \u00e0 tous (MOOC) sur FutureLearn : \u201c De l\u2019ADN au traitement : th\u00e9rapies g\u00e9niques et cellulaires g\u00e9n\u00e9tiquement modifi\u00e9es pour les maladies rares. \u201d<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Coordonn\u00e9 par la FFRD et d\u00e9velopp\u00e9 avec le soutien de l'ASGCT et de la subvention Pfizer Global Medical Education, ce cours rassemble des experts de renomm\u00e9e internationale afin de pr\u00e9senter aux participants les derni\u00e8res technologies qui red\u00e9finissent le paysage m\u00e9dical.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Parmi les th\u00e8mes principaux, on peut citer :<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u00c9dition g\u00e9n\u00e9tique : CRISPR-Cas9, \u00e9dition de bases et \u00e9dition \u00ab prime \u00bb<\/li>\n\n\n\n<li>Th\u00e9rapies \u00e0 base d'ARN : ARNm et oligonucl\u00e9otides antisens (ASO)<\/li>\n\n\n\n<li>Syst\u00e8mes d'administration : vecteurs viraux et syst\u00e8mes non viraux<\/li>\n\n\n\n<li>Impact concret : \u00e9tudes de cas cliniques sur l'h\u00e9mophilie et les troubles m\u00e9taboliques, accompagn\u00e9es de t\u00e9moignages \u00e9mouvants de patients<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">Les inscriptions sont d\u00e9sormais ouvertes : https:\/\/www.futurelearn.com\/courses\/from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">L'acc\u00e8s au contenu est gratuit pendant les 3 premi\u00e8res semaines suivant l'inscription. A<strong> s\u00e9ance anim\u00e9e <\/strong>se d\u00e9roulera du 16 mars au 8 mai. Pendant cette p\u00e9riode, des experts seront disponibles en ligne pour r\u00e9pondre aux questions et accompagner les apprenants en temps r\u00e9el.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Ce cours s'adresse principalement \u00e0<strong>\u00a0\u00e9tudiants universitaires et chercheurs en d\u00e9but de carri\u00e8re dans les domaines de la biologie, des sciences de la vie et de la m\u00e9decine<\/strong>. Il peut \u00e9galement int\u00e9resser les professionnels de sant\u00e9, les d\u00e9cideurs politiques, les repr\u00e9sentants du secteur priv\u00e9, les d\u00e9fenseurs des droits des patients et toute personne souhaitant mieux comprendre le d\u00e9veloppement des th\u00e9rapies g\u00e9niques et cellulaires modifi\u00e9es g\u00e9n\u00e9tiquement destin\u00e9es au traitement des maladies rares. Il est recommand\u00e9 d\u2019avoir des connaissances de base en biologie.<\/p>","protected":false},"excerpt":{"rendered":"<p>With over 95% of rare diseases still lacking approved treatments, there is a pressing need for specialized education in next-generation therapeutics. To address this gap, the Foundation for Rare Diseases (FFRD) is excited to announce the launch of their new Massive Open Online Course (MOOC) on FutureLearn: \u201cFrom DNA to Cure: Gene and Gene-Modified Cell [&hellip;]<\/p>\n","protected":false},"featured_media":0,"template":"","categories":[],"tags":[],"class_list":["post-9413","news","type-news","status-publish","hentry"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v28.8 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>New MOOC Launch: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases - ERN ITHACA<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/ern-ithaca.eu\/fr\/events-news\/news\/new-mooc-launch-from-dna-to-cure-gene-and-gene-modified-cell-therapies-for-rare-diseases\/\" \/>\n<meta property=\"og:locale\" content=\"fr_FR\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"New MOOC Launch: From DNA to Cure \u2013 Gene and Gene-Modified Cell Therapies for Rare Diseases - ERN ITHACA\" \/>\n<meta property=\"og:description\" content=\"With over 95% of rare diseases still lacking approved treatments, there is a pressing need for specialized education in next-generation therapeutics. 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